A Phase III, Randomized, Controlled, Global Multicenter Study to Evaluate the Efficacy and Safety of Oral Tinengotinib versus Physician’s Choice in Subjects with Fibroblast Growth Factor Receptor (FGFR)-altered, Chemotherapy- and FGFR Inhibitor-Refractory/Relapsed Cholangiocarcinoma (FIRST-308)

ClinicalTrials.gov Identifier
NCT05948475
Institution Name
University of Texas MD Anderson Cancer Center
Full Institution Address
1515 Holcombe Blvd, Houston, TX 77030

Houston
Texas
77030
United States
Institution Phone
(877) 632-6789
Institution Website
https://www.mdanderson.org
Additional Institutions
UCLA Medical Center 1-310-829-5471
The University of Chicago Hospitals The University of Chicago Medical Center UCMC 1-773-702-1530
Roswell Park Comprehensive Cancer Center 1-716-716-845-1300×1912
The University of Texas MD Anderson Cancer Center 1-713-794-1226
University of Virginia Cancer Center 1-434-297-5502
SCRI Oncology Partners 1-615-329-6862
Mount Sinai Comprehensive Cancer Center 1-305-535-3300
University of Texas Southwestern Medical Center – University Hospital Medical Oncology Clinic – Gastrointestinal
Stanford Cancer Center
Vanderbilt-Ingram Cancer Center
Henry Ford Health 1-404-778-1900
Medical College of Wisconsin
The University of Kansas Cancer Center 1-913-945-5052
Messino Cancer Center 1-828-212-7021
University of Minnesota- Masonic Cancer Center, M Health Fairview 1-612-624-0123
Texas Oncology-Sammons Cancer Center
UMass Memorial Medical Center 1-774-622-500
Memorial Sloan Kettering Cancer Center 1-646-8884314
Principal Investigator
Milind Javle
Principal Investigator Phone
1-713-794-1226
Principal Investigator Email
mjavle@mdanderson.org
Additional Principal Investigators
Sahai, Vaibhav vsahai@med.umich.edu 1-734-647-8902
Mahipal, Amit amitmahipal@gmail.com
Sadeghi, Saeed ssadeghi@mednet.ucla.edu 1-310-829-5471
Liao, Chih-Yi andyliao@medicine.bsd.uchicago.edu 1-773-702-1530
Fountzilas, Christos christos.fountzilas@roswellpark.org 1-716-716-845-1300×1912
Javle, Milind mjavle@mdanderson.org 1-713-794-1226
Kunk, Paul prk5r@hscmail.mcc.virginia.edu 1-434-297-5502
Pelster, Meredith Meredith.Pelster@sarahcannon.com 1-615-329-6862
Cusnir, Mike Gregory.Ruddell@msmc.com 1-305-535-3300
Hsieh, David david.hsieh@utsouthwestern.edu
Goyal, Lipika lgoyal@stanford.edu
Heumann, Thatcher thatcher.heumann@vumc.org
Diab, Maria mdiab2@hfhs.org 1-404-778-1900
Phan, Alexandria aphan@mcw.edu
Al-Rajabi, Raed ral-rajabi@kumc.edu 1-913-945-5052
Beardsley, Andrew andrew.beardsley@aoncology.com 1-828-212-7021
Greeno, Edward green048@umn.edu 1-612-624-0123
Kitchens, Benjamin benjamin.kitchens@usoncology.com
Martin, Alexander alexander.martin3@umassmemorial.org 1-774-622-500
Harding, James hardinj1@mskcc.org 1-646-8884314
Study Coordinator
Josephine Charles
Study Coordinator Phone
713-750-1488
Study Coordinator Email
JJCharles@mdanderson.org
Additional Study Coordinators
Dippman, Dominique dippmand@med.umich.edu
Becker, Laura beckerl@med.umich.edu
Apale, Charmaine Charmaine.Apale2@UHhospitals.org
Cruz, Adam Adam.Cruz@UHhospitals.org
Jarrett, Andrea andrea.jasaleen.jarrett@uhhospitals.org
Labbaf, Layla Layla.Labbaf@UHhospitals.org
Ruiter, Adam adam.ruiter@uhhospitals.org
Hunt, Alexia AlexiaHunt@mednet.ucla.edu
Chang, Hang hchang@medicine.bsd.uchicago.edu
Torre-Dorado, David ddelatorredorado@uchicago.edu
Krasowski, Marian mariankrasowski@uchicago.edu
Villamar, Dario dmv@uchicago.edu
Berrueco, Luca Luca.Berrueco@bsd.uchicago.edu
Bobb, Tameka tbobb@uchicago.edu
Brooks, Amber xbu5595@uchicago.edu
Desgardin, Aurelie adesgard@uchicago.edu
El-Naggar, Ryan relnaggar@uchicago.edu
Shaik, Afnan ashaik@uchicago.edu
Zubeck, Mia mzubeck@uchicago.edu
Scott, Koya koyas@uchicago.edu
Woodfolk, Asha zxz4798@uchicago.edu
Chatley, Sarah sarah.chatley@roswellpark.org
Farrell, William William.Farrell@RoswellPark.org
Blamowski, Jenna Jenna.Blamowski@RoswellPark.org
Arena, Kathleen Kathleen.Arena@RoswellPark.org
House, Alexandra alexandra.house@roswellpark.org
Cox, Cimetra crcox@mdanderson.org
Charles, Josephine JJCharles@mdanderson.org
Harris, Kristen kah2gv@virginia.edu
Flanagan, Cecilia cnr7zp@hscmail.mcc.virginia.edu
James, Olivia omj5cg@hscmail.mcc.virginia.edu
Neider, Amanda ALN4K@hscmail.mcc.virginia.edu
George, Jessy jrg9n@uvahealth.org
Du, Kevin kmd3pj@virginia.edu
Brennan, Emma Emma.Brennan@scri.com
King, Lauren lauren.king@scri.com
Trull , Ethan ethan.trull@sscri.com
Miller, Alydia 615-329-7274
Goya Balaguer, Evelyn Evelyn.goyabalaguer@msmc.com
Lacombe , Ana Ana.Lacombe@msmc.com
Brauchle, Yelida yelida.brauchle@msmc.com
Hahn, Kaitlin kaitlin.hahn@msmc.com
Welsh, Madeleine welshm@stanford.edu
Puri, Shipra spuri1@hfhs.org
Didevich, Dimitry ddidevi1@hfhs.org
Heaviland, Haley hheavila@mcw.edu
Molloy, Shannon smolloy@mcw.edu
Dion, Barbara badion@mcw.edu
Vallandingham, Ashley avallandingham@kumc.edu
Cochran, Peggy pcochran@kumc.edu
Duckett, Josh Josh.Duckett@aoncology.com
Barrett, Chelsea Chelsea.Barrett@SarahCannon.com
Soper, Stephanie ssoper@umn.edu
Ford, Katreece katreece.ford@usoncology.com
Agrilo, Alexandra Alexandra.Agrillo@umassmed.edu
Malone, Paige Paige.Malone@umassmed.edu
Study Overview
This is a Phase 3 trial of the targeted therapy tinengotinib in cholangiocarcinoma. Tinengotinib is a new FGFR inhibitor which targets FGFR2 fusions and rearrangements, and has been shown to be effective after a patient receives another FGFR inhibitor such as pemigatinib. This study is randomized in a 2:1 ratio (tinengotinib:control), with the control arm being the chemotherapy thought to be the best fit for the patient.
Enrollment Information
Open
Study Start Date
2023-12-01
Study End Date
2026-04-01
Study Purpose
+ To evaluate the effectiveness of tinengotinib in extending a patient's time on treatment without progressive disease
+ To evaluate the effectiveness of tinengotinib in extending a patient's life overall
+ To evaluate the safety of tinengotinib
+ To evaluate the quality of life of a patient receiving tinengotinib compared to standard of care therapy
Inclusion Criteria
+ Histologically or cytologically confirmed CCA/adenocarcinoma of biliary origin with radiological evidence of unresectable or metastatic disease.
+ Documentation of FGFR2 fusion/rearrangement gene status. Documentation from any point in disease course since the time of initial diagnosis is acceptable
+ Subjects must have received at least one line of prior chemotherapy and exactly one FDA-approved FGFR inhibitor (pemigatinib, infigratinib or futibatinib . Documentation of disease progression or recurrence following prior systemic chemotherapy and FGFR inhibitor therapy. Systemic adjuvant chemotherapy will be considered a line of treatment if there is documented disease progression or recurrence during or within 6 months of completing the therapy.
+ Radiographically measurable disease
Exclusion Criteria
+ Prior receipt of two or more FGFR inhibitors, either approved or investigational drugs.
+ Prior receipt of both FOLFOX and FOLFIRI chemotherapy regimens [+ v2.1].
+ Have known brain or central nervous system (CNS) metastases that have radiologically or clinically progressed in the 28 days prior to initiation of therapy
+ Have uncontrolled hypertension (defined as blood pressure of ≥150 mm Hg systolic and/or ≥ 90 mm Hg diastolic despite adequate treatment with antihypertensive medications at Screening).
Financial Assistance Available
Yes